Fatty Acid Oxidation DisordersNewborn ScreeningRUSP

Long-Chain 3-Hydroxyacyl-CoA Dehydrogenase Deficiency

LCHADD

LCHADD is part of the mitochondrial trifunctional protein pathway and causes hypoketotic hypoglycemia, peripheral neuropathy, and retinopathy in some patients. Dietary fat modification, avoidance of fasting, and specialized follow-up are required. Early detection through screening improves outcomes before irreversible complications.

Prevalence
1 in 250,000
Inheritance
Autosomal recessive
Screened at Birth
Yes
On RUSP
Yes (Recommended Uniform Screening Panel)

About This Data

This disorder is part of the Cureledger rare disease data corpus. We are building privacy-preserving natural history datasets and advocacy tools for rare disease communities. Data is maintained by clinical advisors and the patient community.